Carotti, M., Marsolier, J., Soardi, M., Bianchini, E., Gomiero, C., Fecchio, C., … Sandonà, D. (2018). Repairing folding-defective α-sarcoglycan mutants by CFTR correctors, a potential therapy for Limb Girdle Muscular Dystrophy 2D. Human Molecular Genetics. https://doi.org/10.1093/hmg/ddy013 (Original work published 2018)
R Betto
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R
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Betto